HOW CAN WE HELP YOU? Call 1-800-TRY-CHOP
DCA Trial in PDC Deficiency
This study is now recruiting.
We are studying an investigational drug called sodium dichloroacetate (DCA). Investigational means that the study drug has not been approved by the US Food and Drug Administration (FDA) and that its use in this study is experimental. This a purpose of this research study is to determine whether DCA is a helpful treatment for patient with pyruvate dehydrogenase complex (PDC) deficiency (PDCD).