Gene Editing | CHOP Research Institute

Gene Editing

Published on
May 10, 2024
This week, honors for innovative CHOP investigators, early results of gene editing for inherited blindness, plus ASGCT and PAS meeting highlights.
Published on
Mar 14, 2024
During Women’s History Month, student intern Sarai Sales reflects on women who have empowered her to further her career.
Published on
Feb 28, 2024
William Peranteau, MD, along with CHOP and Penn researchers are developing “one-and-done” new base-editing therapies for three genetic diseases of newborns.
Published on
Sep 1, 2023
This week’s news roundup features three studies, Doris Duke Award winners, and a commitment to the CHOP Parkway Run & Walk.
Published on
Jul 31, 2023
Researchers developed a proof-of-concept model for delivering gene editing tools to treat blood disorders, allowing for the modification of diseased blood cells directly within the body.
Published on
Feb 3, 2023
In this news roundup, we celebrate research tools new and old, from RNA sequencing to gene editing to the best tool of all: collaboration.
Published on
May 26, 2021
The 17th Research Institute Scientific Symposium, held virtually on May 20, highlighted advances in cell and gene therapy.

Individuals with beta thalassemia that is treated with regular transfusions, and who are between the ages of 18 and 40 years old, may be able to participate.

The Human Pluripotent Stem Cell Core provides services for the development of novel, human cell-based experimental models for elucidating the pathophysiology of genetic disorders.

Published on
Oct 21, 2019
Join us in congratulating cell and gene therapy experts Beverly Davidson, PhD, and Stephan Grupp, MD, PhD, newly elected to the National Academy of Medicine.