Results for Spinal Muscular Atrophy

1 - 8 of 8

Dr. Baldwin is an orthopaedic surgeon who specializes in the treatment of traumatic, neuromuscular, and spinal conditions in children.

E-mail:

baldwink [at] chop.edu

Optimizing Vector Delivery to Reduce Risk: Q&A With Beverly Davidson, PhD, and Misun Hwang, MD

Published on

Feb 6, 2023

in Cornerstone Blog

Gene Therapy and Radiology Team Up to Optimize Vector Delivery

Two scientists with unique skill sets are developing an alternative method for gene therapy delivery with support from a CGTC Seed Grant.

New Innovator Award Advances Research in Prenatal Gene Editing to Treat Congenital Disorders

Published on

Jan 14, 2020

in Cornerstone Blog

William Peranteau, MD, receives NIH grant to study in utero gene editing treatment for congenital monogenic disorders.

Making Time for Science: Meet Jaxson and Megan, Research Hero and Super Mom

Published on

May 12, 2019

in Cornerstone Blog

We’re celebrating our research hero, Jaxson, and his super mom, Megan, this Mother’s Day. Thank you for making time for science.

Progression of SMA

The purpose of this study is to collect data from routine standard of care visits of SMA patients at the Children's Hospital of Philadelphia Neuromuscular Clinic.

Division of Neurology

Child Neurology at CHOP is home to world-class integrated clinical, translational, and basic neuroscience research focused on neurological conditions in children and adolescents.

Gene and Cell Therapy Clinical Trials

Find research studies conducted by the Clinical In Vivo Gene Therapy group.

Intellectual and Developmental Disabilities Research Center

In advancing intellectual and developmental disabilities (IDD) research for more than 29 years, the Intellectual and Developmental Disabilities Research Center (IDDRC) wholeheartedly embraces today’s novel concepts and technologies to discover the causes of IDD and uses this knowledge to improve outcomes for affected people.