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Snapshot Science: How Did Researchers Resolve Adverse Symptoms that Emerged with AAV-based RNA Interference Strategies for Ataxia Therapy?
Oct 18, 2021
Raymond G. Perelman Center for Cellular and Molecular Therapeutics team highlights that extended safety testing of AAV-based RNAi strategies is critical.
Researchers Fine-tune Disrupted Brain Circuitry With Focal Gene Therapy
Oct 29, 2020
Chemogenetic technology is making it more possible to identify abnormal circuitry, correct it, and change the relevant behaviors.
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