Clinical In Vivo Gene Therapy Team



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Led by experts in in vivo gene therapy research, with more than 10 years of clinical trial experience, the Clinical In Vivo Gene Therapy team has a wealth of knowledge to navigate the complex safety, regulatory, and clinical care considerations of gene therapy clinical research.

Lindsey A. George

Lindsey A. George, MD

Tenure Assistant Professor of Pediatrics, Perelman School of Medicine, University of Pennsylvania

Dr. George's basic and clinical research interests are in the development of novel therapeutics for hemophilia. Her basic science laboratory studies the molecular basis of coagulation, and she is the principal investigator of ongoing hemophilia A and B gene therapy trials.


Amy Waldman, MD, MSCE
Associate Director for Neurology Gene Therapy

Sarah McCague, MS
Clinical Research Program Manager

Juliana Small, PhD
Regulatory Affairs Translational Specialist

Julianne LaRosa, MPH
Clinical Research Coordinator

Jasmine Hanks, BA
Clinical Research Coordinator